Gene therapy successes point to better therapies
Elie Dolgin • November 26, 2019
Despite some data concerns, two treatments for a rare pediatric killer could usher in a new wave of innovative medicines for neurological conditions.
Continue reading at PNAS.
With organoids, assembloids and a growing bioengineering toolkit, scientists are pushing the limits of human brain models.
Drug makers are scrambling to navigate an ‘existential threat’ to a once-celebrated technology.